The US Food and Drug Administration (FDA) has approved Dawnzera (donidalorsen) for prophylaxis to prevent attacks of ...

The approval makes donidalorsen the only treatment in the US for hereditary angioedema that is an RNA-targeted prophylactic.

On Thursday, the U.S. Food and Drug Administration (FDA) approved Ionis Pharmaceuticals, Inc.’s (NASDAQ:IONS) Dawnzera ...

The collaboration will explore RNA-based small molecule drug candidates aimed at neurological conditions where existing ...

To our immune system, naked RNA is a sign of a viral or bacterial invasion and must be attacked. But our own cells also have ...

Yale researchers have developed a new and safe family of RNA-editing tools that utilize an RNA-targeting activity that they ...

In June, the monoclonal antibody garadacimab (Andembry) was approved for prevention of HAE attacks at a dose of once monthly ...

Sarepta is facing a number of issues currently, including platform-level safety concerns, management credibility issues, etc.

The ability to correct disease-causing genetic mistakes using genome editors holds great promise in medicine, but it is not ...

In 1957, just four years after Francis Crick and other scientists solved the riddle of DNA’s structure—the now famous double ...